Afaceri specificat Grozav dm1 gene speranţă Monarh include
Model for the molecular consequences of triplet expansion in DM1. In... | Download Scientific Diagram
RNA toxic gain-of-function model for DM1 pathogenesis. Mutant DMPK RNA... | Download Scientific Diagram
Specific DMPK-promoter targeting by CRISPRi reverses myotonic dystrophy type 1-associated defects in patient muscle cells: Molecular Therapy - Nucleic Acids
Application of CRISPR-Cas9-Mediated Genome Editing for the Treatment of Myotonic Dystrophy Type 1: Molecular Therapy
DM1-AS Gene - GeneCards | DM1-AS RNA Gene
DM1 pathogenetic mechanisms and therapeutic strategies. The actions of... | Download Scientific Diagram
Entrada Therapeutics | Myotonic Dystrophy Type 1 (DM1)
W David Arnold - Myotonic Dystrophy Overview and Update
Cardiovascular manifestations of Myotonic Dystrophy
Best practice guidelines and recommendations on the molecular diagnosis of myotonic dystrophy types 1 and 2 | European Journal of Human Genetics
Myotonic dystrophy: candidate small molecule therapeutics - ScienceDirect
Myopathies without EOM Weakness: Facioscapulohumeral + Myotonic Dystrophy
IJMS | Free Full-Text | Epigenetics of Myotonic Dystrophies: A Minireview
Comprehensive transcriptome-wide analysis of spliceopathy correction of myotonic dystrophy using CRISPR-Cas9 in iPSCs-derived cardiomyocytes: Molecular Therapy
RNA toxicity model for DM1 pathogenesis and potential therapeutic... | Download Scientific Diagram
Molecular genetics of congenital myotonic dystrophy - ScienceDirect
Epigenetics and Myotonic Dystrophy Type 1 | Encyclopedia MDPI
Projects
IJMS | Free Full-Text | Disrupting the Molecular Pathway in Myotonic Dystrophy
Frontiers | Muscle wasting in myotonic dystrophies: a model of premature aging
Aberrant Expression of a Non-muscle RBFOX2 Isoform Triggers Cardiac Conduction Defects in Myotonic Dystrophy - ScienceDirect
Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene: Molecular Therapy - Nucleic Acids
Myotonic dystrophy - Wikipedia
Myotonic Dystrophy Testing & Diagnosis | Myotonic Dystrophy Foundation
Strategies for DM1 gene therapy. A) Degradation of mutant RNA by... | Download Scientific Diagram
Gene Therapy and Gene Editing for Myotonic Dystrophy | SpringerLink
IJMS | Free Full-Text | Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing